A 19-year-old Canadian man becomes the first human cured through prime gene editing after doctors corrected a rare genetic ...

A new method for safely inserting large chunks of DNA into genomes has now measured up in mice, potentially paving the way ...

Lipid nanoparticles, or LNPs, best known as the delivery vehicle for the COVID-19 mRNA vaccines received by billions of people, are now at the center of a much larger medical revolution. Researchers ...

After teasing a new regulatory process for personalized genetic medicines at the end of last year, the FDA today unveiled draft guidance for an approval pathway that could see custom CRISPR therapies, ...

Drug delivery researchers have vastly improved the potential of genetic therapies by overcoming the challenge of consistently getting genes and gene-editing tools where they need to be within cells.

Prime Medicine's application will test an FDA that has promised to speed new gene-editing treatments but has recently spurned ...

Gene editing, a set of techniques used to alter sections of an organism's DNA, is helping scientists cure diseases previously ...

The U.S. Food and Drug Administration approved the first cell-based gene therapies for sickle cell disease, including the ...

Scientists at Texas A&M are turning an everyday pick-me-up into a high-tech medical switch. By combining caffeine with CRISPR ...

Scientists are testing an entirely new way to fight heart disease: whether gene editing might offer a one-time fix for high cholesterol.

UCLA researchers use lipid nanoparticles to insert full CFTR gene into airway cells, restoring function and opening new avenues for CF therapy.

Scientists generate world’s first ’extraordinary aromatic tomato plants’ by simultaneously altering two key genes ...