LONDON -- A 3-year-old girl who underwent a breakthrough gene therapy treatment to treat profound hearing loss can hear on ...

Up to 60% of congenital and early-onset hearing loss is caused by genetic mutations in an inherited gene, and gene therapy ...

“Beyond UniQure, the pipeline includes highly promising approaches that will ideally move the goal from merely managing ...

When she was born, doctors informed Opal Sandy’s parents that their child would never hear. At the age of 11 months, she had ...

Miracles happen every day, everywhere, in scenarios we can hardly imagine.Although human life has become so complex that we ...

On her mother’s instruction, a toddler gives her pink stuffed horse, Snap Snap, a big cuddle. Then, as told, she plants a kiss on his soft fur and, because he’s hungry, feeds him a pretend bowl of ...

These results are what we hoped for when we first began developing this approach,' one researcher said. View on euronews ...

In February, the biotech reported improvements in 10 of 11 children who received DB-OTO. The AAV gene therapy, which ...

In a note to investors on Sunday, analysts at Leerink Partners called these findings “compelling,” adding that they indicate ...

Study results published in The New England Journal of Medicine show the therapy significantly improved hearing in nearly a ...

A one-time subretinal injection of Sura-vec at both high- and low-dose concentrations allowed more than half of patients with ...

Up to 60% of congenital and early-onset hearing loss is caused by genetic mutations in an inherited gene, and gene therapy ...