A new gene therapy approach aimed at protecting people with type 1 diabetes from developing diabetic kidney disease—a serious ...

University of Bristol researchers have discovered a VEGF-C gene therapy that protects the kidneys in people with type 1 ...

Gene therapy is linked to better nonmotor outcomes in spinal muscular atrophy type 1 compared to first-line nusinersen, new ...

In a preclinical mouse study, gene therapy delivering VEGFC to kidney cells reduced early signs of kidney damage in Type 1 ...

An experimental gene therapy developed by researchers at UCLA, University College London and Great Ormond Street Hospital has ...

For children born with severe combined immunodeficiency due to adenosine deaminase deficiency (ADA-SCID), an investigational ...

The cell and gene therapy drug delivery market plays a pivotal role in advancing precision medicine by ensuring the effective introduction of living cells and genetically modified genes into patients.

The goal of gene therapy is to permanently cure hereditary diseases. One of the most promising technologies for this is the ...

A new study has brought scientists one step further in the direction of developing a cure for a brutal group of rare brain ...

New research found that gene therapy for children with "bubble boy disease," or SCID, was successful in 95% of trial ...

A single one-time gene therapy could free patients with α-thalassemia, a rare and debilitating blood disorder, from the burden of lifelong transfusions. A single one-time gene therapy could free ...

The novel treatment, partly developed by CHOP, eliminates the need for regular infusions while preventing the ...