A new study has brought scientists one step further in the direction of developing a cure for a brutal group of rare brain ...

MIT scientists have found a way to make gene editing far safer and more accurate — a breakthrough that could reshape how we ...

The global cell and gene therapy market is undergoing rapid expansion, driven by the surge in regulatory approvals and continual advancements in therapeutic technologies. The market is anticipated to ...

Moorfields Eye Hospital in London made international headlines last week. Doctors announced they had saved the sight of four young children suffering from a rare genetic condition that rapidly causes ...

Researchers in Göttingen, Germany, have elucidated the structure and function of otoferlin, a protein that plays a crucial ...

Immusoft of CA, a clinical-stage biotechnology company pioneering engineered B cell therapies, today announced that the U.S. Food and Drug Administration (FDA) has granted Fast Track designation to ...

Researchers have achieved the first demonstration in mice of using gene therapy to reverse hallmark symptoms of ...

Out of the shadows, new CDMO Artis BioSolutions has decloaked on a mission to tackle the tricky production process for advanced therapeutics. Artis officially emerged from stealth on Wednesday, ...

Research Ireland and APC will together fund new research into how advanced gene therapies are created and delivered.

Scientists have reversed diabetic heart failure with a genetic therapy in mice and miniature human "hearts" grown from stem ...

Venture capital investment in gene therapies fell to $1.4 billion in 2024 from 2021 peak of $8.2 billion Total global biopharma venture funding rose to $27 billion in 2024 from $23.2 billion in 2023 ...

Twenty-six years ago today, on Sept. 17, a teenager who had received an experimental gene therapy died. His death led to needed changes in the clinical trial process while also spurring skepticism ...