Gene therapy is becoming a powerful way to treat challenging diseases that don’t respond to traditional treatments, and researchers now report the first success in modifying genes to slow Huntington’s ...
Scientists have slowed the progression of Huntington’s disease for the first time with a “groundbreaking” new treatment. Experts from University College London (UCL) said the finding could “change ...
Sex influences how genetic and age-related factors translate into clinical and neuroimaging trajectories in Huntington disease.
ST. LOUIS — Scientists may have reached a breakthrough in the fight against Huntington’s disease, a rare and fatal inherited brain disorder with no cure. For the first time, a gene therapy has been ...
An experimental gene therapy was found to slow the progression of Huntington's disease in a "pivotal" Phase 1/2 study, according to drugmaker uniQure, marking a major step toward a potential first ...
UCL and uniQure report the first treatment to slow Huntington’s disease with gene therapy AMT-130. High-dose patients had 75% less progression over three years compared with standard care. uniQure ...
Huntington’s disease is a fatal, hereditary neurological disorder mostly striking people between the ages of 30 and 50. In 1872, a young physician, Dr. George Huntington, first described the disease ...
TAMPA, Fla. (WFLA) — For the first time, scientists have successfully treated someone suffering from Huntington’s disease, a fatal genetic illness with no cure. The Mayo Clinic reports that the ...