Britain's medicines regulator has authorized the world's first gene therapy treatment for sickle cell disease, in a move that could offer relief to thousands of people with the crippling disease in ...

A one-time gene-editing therapy, exagamglogene autotemcel (exa-cel), has demonstrated sustained and clinically meaningful ...

People are often encouraged to “know their status,” however this healthy habit can be applied to more than just safe-sex practices. Although they are not the only community who suffers with sickle ...

Sickle cell disease refers to a group of genetic diseases that impact a protein that ferries oxygen through the blood. That protein is called hemoglobin, and in sickle cell disease, aberrant ...

Gene therapy has the potential to dramatically benefit patients with genetic blood disorders, but a small study on participants in a clinical trial for sickle cell disease suggests that a key process ...

Life expectancy has soared and interest in the disease is growing, but breakthrough gene therapies are extraordinarily ...

The federal approval of two new gene therapy treatments for sickle cell disease has created a groundbreaking option for patients. Across the nation, it is unknown how many suffer from the disease, but ...

Federal officials Friday approved two gene therapy treatments for sickle cell disease, welcome news for tens of thousands with the inherited blood disorder that causes terrible pain crises and early ...

Sickle cell disease (SCD) is an inherited disorder that affects over 100,000 people in the United States, according to the Sickle Cell Disease Association of America, of that number, the Centers for ...

A parasite that causes malaria is halted by sickle cells and makes people who carry the sickle cell trait more resistant to the disease. This is why sickle cell trait also occurs more in people who ...

Researchers have found that being a carrier for sickle cell disease, known as having sickle cell trait, increases the risk of blood clots, a risk that is the same among diverse human populations that ...

The only cure for painful sickle cell disease today is a bone marrow transplant. But soon there may be a new cure that attacks the disorder at its genetic source. On Tuesday, advisers to the Food and ...