Columnist Helen Baldwin has always been drawn to caring for those who need a little extra help, be it a shelter dog or a baby with SMA.

Newborn screening for SMA enables significantly earlier initiation of disease-modifying treatments. Early treatment was associated with motor function and development in infants with SMA. Prenatal ...

Clinical & Scientific Conference, researchers and clinicians are talking about the central role of patients, families, and caregivers in driving change for people living with neuromuscular diseases.

Biogen has launched a trio of Phase 3 trials to test salanersen, a new SMA treatment that aims to be a more convenient ...

Apitegromab improved motor function in SMA patients in a Phase 3 trial analysis, with stronger benefits seen in those treated earlier.

A new study found Spinraza treatment restores a key amino acid called taurine in SMA type 1, which may improve clinical ...

Medical equipment and technology are crucial for columnist Ari Anderson, who lives with SMA, so malfunctions can quickly ...

Spinraza treatment led to sustained improvements in motor function in adults with SMA, according to a South Korean study.

The first patient has been dosed in a Phase 1/2 study of GB221, a next-generation gene therapy for SMA type 1.

Today is Caregiver Appreciation Day and columnist Connie Chandler wants the caregivers in her life to know how much she appreciates them.

For columnist Sherry Toh, the new TV series "The Beauty" dwells too much on the grief of living with a rare disease but ignores the strength.

Scholar Rock plans to resubmit its application seeking approval for apitegromab, an investigational muscle-strengthening therapy for SMA.