Genethon, a pioneer and leader in gene therapy for rare diseases, unveiled results at the MDA Conference in Orlando confirming the long-term efficacy of its GNT0004 gene therapy in Duchenne muscular ...

Full Circles Therapeutics today announced that its circular single-stranded DNA (cssDNA, C4DNAtm) technology platform has been highlighted as a key enabling component of a new genome engineering ...

A settlement is reached in the case of Mike Disfarmer, who renounced his family. Decades later they sued to take back his life’s work. When heirs battle the people who built their legacies, the art ...

Investigational RGX-202 continues to demonstrate evidence of positively changing disease trajectory for Duchenne Pivotal dose participants exceeded external controls across functional ...

We’ve already been treated to an amazing first half of the year, concert-wise, but artists aren’t letting up yet; 2025 has some mammoth stadium and arena gigs still in store. Last year was defined by ...