3-year-old born deaf can hear 2 years after breakthrough gene therapy treatment

A 3-year-old girl who underwent a breakthrough gene therapy treatment to treat profound hearing loss can hear on her own, two ...
The Brighterside of News on MSN

Toddler born deaf hears for the first time after groundbreaking gene therapy

When she was born, doctors informed Opal Sandy’s parents that their child would never hear. At the age of 11 months, she had ...

Lisa Jarvis: A new gene therapy for a rare form of congenital deafness looks promising

The trial was small — just 12 children were treated in one or both ears — but it offers important lessons for researchers ...
Healio

‘One-and-done’ gene therapy could shift wet AMD treatment paradigm

A one-time subretinal injection of Sura-vec at both high- and low-dose concentrations allowed more than half of patients with ...

International experts produce guidelines for treating hereditary hearing loss with gene therapy

Up to 60% of congenital and early-onset hearing loss is caused by genetic mutations in an inherited gene, and gene therapy ...
News Medical on MSN

Gene therapy delivers lasting immune protection in children with rare disorder

Long-term follow-up shows 95% success rate, no serious complications in largest ADA-SCID gene therapy study to date ...
Fierce Biotech

Regeneron amplifies CHORD progression, sharing updated data on hearing loss gene therapy

In February, the biotech reported improvements in 10 of 11 children who received DB-OTO. The AAV gene therapy, which ...
News-Medical.Net on MSN

International experts publish guidelines on the administration of gene therapy for hereditary hearing loss

Up to 60% of congenital and early-onset hearing loss is caused by genetic mutations in an inherited gene, and gene therapy ...

Scientists may have discovered first gene therapy for incurable brain disease

Researchers announce breakthrough results for AMT-130, the first disease-modifying treatment for Huntington's disease, with ...

Experimental gene therapy successfully treats dozens of children with rare fatal disorder

These results are what we hoped for when we first began developing this approach,' one researcher said.View on euronews ...
Study Finds

Gene Therapy Breakthrough: Single Treatment Reverses Symptoms In Mouse Model Of Rare Brain Disorder

Researchers have achieved the first demonstration in mice of using gene therapy to reverse hallmark symptoms of ...