Genome editing-based therapies typically aim to treat disease by correcting underlying genetic mutations in patient's cells.

Genetic diseases are notoriously challenging to treat, especially when each condition requires a tailored approach. With over 10,000 known genetic disorders, developing individual therapies for each ...

A closer examination of the APOL1 gene in Black patients with kidney disease can provide more accurate diagnoses than current ...

A new method for safely inserting large chunks of DNA into genomes has now measured up in mice, potentially paving the way ...

A researcher suggests cancer may be influenced by metabolism rather than genetics alone. Learn how glucose, glutamine, mitochondria, and blood sugar levels may affect tumour growth and cancer ...

Cannabis and other illicit drugs are associated with higher stroke risk, underscoring the importance of addressing substance ...

The drug leucovorin was touted by the Trump administration in September as a potential treatment for thousands of children with autism. Now, some parents and guardians of children with autism say they ...

Eisai will present lecanemab data focused on real-world efficacy and safety, as well as four-year data from the Clarity AD Open-Label Extension trial. Eisai will also host one industry-sponsored ...

Yentli Soto Albrecht, who is a genetic carrier of ALS, is working on research at Penn that could one day prove life-saving.

FDA worked with GSK to update Wellcovorin labelling for safe, effective use in adult and paediatric CFD-FOLR1 patients.

This year’s Rare Disease Day event Feb. 27 at the Jacobs School of Medicine and Biomedical Sciences focused on updates in research and diagnostics, and advancements in treatment.