The FDA proposes new rules allowing mutation-specific gene therapies to qualify for approval despite extremely small patient ...

Genome editing-based therapies typically aim to treat disease by correcting underlying genetic mutations in patient's cells.

Genetic diseases are notoriously challenging to treat, especially when each condition requires a tailored approach. With over 10,000 known genetic disorders, developing individual therapies for each ...

The Israeli Basket of Health Services now includes preimplantation genetic testing and in vitro fertilization (PGT-IVF) for individuals carrying three specific genetic markers.

A closer examination of the APOL1 gene in Black patients with kidney disease can provide more accurate diagnoses than current ...

A new method for safely inserting large chunks of DNA into genomes has now measured up in mice, potentially paving the way ...

Mayo Clinic researchers have identified a rare mutation in the MET gene that can directly cause metabolic dysfunction-associated steatotic liver disease. The mutation disrupts the liver’s ability to ...

Donor candidates have to be aged 18 to 60, blood type 0, in good general health, and be willing to undergo screening.

A new study published in Neurology, led by Queen Mary University of London, has revealed that people of South Asian, African ...

A new federal proposal aimed at speeding approval of gene therapies for ultra-rare diseases could offer renewed hope to North Texans like Kasey and ...

Doctors warn that Bulgaria’s healthcare system still lacks a sustainable framework for genomic diagnostics, patients are paying the price ...

A researcher suggests cancer may be influenced by metabolism rather than genetics alone. Learn how glucose, glutamine, mitochondria, and blood sugar levels may affect tumour growth and cancer ...