An FDA complete response letter for idebenone in LHON indicates unresolved NDA deficiencies and necessitates additional data before approval can be reconsidered. Priority review status and a February ...

The first group of patients in the GS010 AAC program were treated at the 15-20 National Hospital in Paris on March 19. The REVISE dose-ranging study is proceeding according to the planned ...

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Longtime Board member, parent advocate, and business executive slated to guide next phase of the organization's growth and mission, effective immediately. COLUMBIA, Md., March 12, 2026 /PRNewswire/ -- ...

Great Britain's Hester Poole is setting her sights on Saturday's slalom after crashing out of the giant slalom on her Winter ...

The biotech could run out of funding before it can launch a single product.

Service dogs can help make the impossible paw-sible. As 665 athletes prepare for the Milano Cortina 2026 Paralympic Winter ...

Hester Poole learns tough lesson in Winter Paralympics debut – but British teenager has hope for the future - Poole fell ...

If she was not already, Hester Poole is now acutely aware that the slopes of the Winter Paralympics show no mercy.

Favorable early safety and initial efficacy data from BEST1 program highlighted at premier gathering of global retinal experts with additional ...

A bill that would remove the religious exemption for skipping the measles vaccine and make it mandatory for attending South Carolina public schools was killed by Statehouse conservatives. The ...