Victoria Gray spent 34 years battling the debilitating pain of sickle cell disease. Then she volunteered to be the world's first "prototype" for a CRISPR therapy, based on technology invented at UC ...
The startup aims to create a platform for treating extremely rare genetic mutations, armed with CRISPR advances and new regulatory pathways.
A pioneering gene therapy for inherited blood disorders has been given to a patient in the UAE for the first time. Known as Casgevy, the potentially life-changing treatment involves deactivating a ...
Aurora Therapeutics, cofounded by Nobel Prize–winning scientist Jennifer Doudna, plans to use gene editing and a new FDA ...
In a world where the immune system can be both hero and villain, three scientists have illuminated the path to taming its excesses. On October 6, 2025, ...