‘Orphan’: First Trailer For László Nemes’ Venice Film Festival Drama & Hungarian Oscar Hopeful

EXCLUSIVE: Deadline can reveal the first trailer for László Nemes’ post-World War II Hungarian family drama Orphan, which ...
Democrat and Chronicle

Jaguar Health Submits Orphan Drug Designation Application to FDA for Crofelemer for Cancer Therapy-Related Diarrhea (CTD) in Patients with Breast Cancer with Metastasis ...

Potential treatment for patients with breast cancer with metastasis to the brain with crofelemer would augment the significant responder analysis results for crofelemer in the prespecified subgroup of ...
InkFreeNews

Bishop Luers First US High School To Perform ‘Orphan Train’

FORT WAYNE — Bishop Luers High School made history this past weekend with its performances of the musical Orphan Train — as the first high school in the United States to perform this musical. Orphan ...
Hosted on MSN

My family are all alive - but I'm still an orphan

Standing outside my mother’s flat, I waited to see if she’d answer the door. Less than 24 hours earlier, I’d run away from her and from this place – a house that was as much a home to me as a jail ...
NDTV

Firm Behind Cough Syrup Linked To Child Deaths Under Scanner In Rajasthan

The company whose cough syrup has been linked to three deaths and a doctor losing consciousness in Rajasthan is now under the state government's scanner. The administration has ordered a thorough ...
ophthalmologytimes

AAVantgarde’s AAVB-039 gene therapy to treat Stargardt disease receives orphan drug status from FDA

AAVB-039 targets Stargardt disease by delivering the full-length ABCA4 protein, addressing the genetic cause of the condition. The FDA granted Orphan Drug and Fast Track Designations, while the UK's ...
Daily

Probe Launched Against Rajasthan Pharma Firm Over Dextromethorphan Syrup-Linked Death

Jaipur: The death of a five-year-old boy in Sikar district has raised serious concerns about the safety of a cough syrup manufactured by Kaysons Pharma, prompting the Rajasthan health department to ...
Toronto Star

AAVantgarde Announces FDA Orphan Drug Designation and UK CTA approval for AAVB-039 for the Treatment of Stargardt Disease

AAVB-039 addresses the root cause of the disease, benefitting patients with any ABCA4 mutation AAVB-039 is currently being assessed in the CELESTE interventional clinical trial and we continue ...
News Medical

The World Orphan Drug Congress Europe heads to Amsterdam for the first time, uniting experts and leaders from rare disease research, patient advocacy, biotech, and pharma to ...

For the first time ever, the World Orphan Drug Congress Europe is heading to Amsterdam, bringing together over 2,000 attendees from around the world to explore the latest advancements, opportunities, ...
The Inlander

Upcoming events in Coeur d’Alene and Spokane Valley offer chances to learn about the gifts of grains: whiskey

Practice, practice, practice. The phrase is typically associated with athletic and artistic endeavors, but no matter the subject, the long version is: The more one practices, the better one gets. It’s ...
KREM

Police: Elderly Coeur d'Alene woman expected to die after attack at home

COEUR D'ALENE, Idaho — An elderly woman who was attacked at home last month is expected to die from her injuries, according to the Coeur d’Alene Police Department, meaning the ongoing investigation ...