The global cell and gene therapy market is undergoing rapid expansion, driven by the surge in regulatory approvals and continual advancements in therapeutic technologies. The market is anticipated to ...

Some genetic disorders—such as cystic fibrosis, hemophilia and Tay Sachs disease—involve many mutations in a person's genome, ...

A one-time gene-editing therapy, exagamglogene autotemcel (exa-cel), has demonstrated sustained and clinically meaningful ...