Gus and Emily Forrester's daughter Leni has Sanfilippo syndrome, a neurodegenrative disease that affects one in 70,000 ...

Gus and Emily Forrester's daughter Leni has been diagnosed with Sanfilippo disease, a genetic condition for which there is currently no treatment in the UK.

Danish drugmaker Novo Nordisk won FDA approval Thursday for a higher dose of its weight-loss drug Wegovy — a decision FDA Commissioner Marty Makary touted on social media because it is the fourth drug ...

AN “invasive” outbreak of the disease has left two dead in Canterbury, Kent, as officials race to curb the “fast-acting” ...

IntraBio Inc. today announced the submission of a supplemental New Drug Application (sNDA) to the U.S. Food and Drug Administration (FDA) for levacetylleucine for the treatment of ...

Two people have died out of 15 cases of bacterial meningitis at the University of Kent in England, and students are being ...

Major aid donors including the United States and Britain are overhauling their relationships with the developing world ...

Ava, Olivia, and Landon Langenhop were all born with a rare and life-threatening immune disorder called severe leukocyte adhesion deficiency-I, or LAD-I. This rare genetic condition makes them at risk ...

This picture invariably brings tears to my eyes. It could be the logo, literally and metaphorically, for current health care policy.

A woman says a volleyball accident revealed a rare genetic condition that leaves her with 13 tumors. McKinnon Galloway, 33, ...

A deadly meningitis outbreak has been reportedly declared a "national incident". Two people have died as the "unprecedented" ...

Thousands of students offered vaccines in bid to stem ‘explosive’ meningitis - Health chiefs said they have not seen an ...