Genentech has stopped developing emugrobart after trial results showed no consistent benefit when added to Evrysdi in people ...

In 2018, when Nell Choi was 9 years old, she began experiencing symptoms that led to hospitalization and a diagnosis of ...

Columnist Sherry Toh usually cringes at people who stare, but a performative art project taught her something new about ...

The movement-related benefits of Itvisma were maintained or continued to deepen over about 15 months after treatment, trial ...

Up to three years of Evrysdi treatment appears safe and may help presymptomatic children with SMA reach and maintain key milestones.

High doses of Spinraza may help stabilize or improve motor function for many people with SMA, per pooled clinical trial ...

Kevin Schaefer (he/him) is a writer, podcaster, and lover of all things pop culture. Diagnosed with SMA type 2 at the age of 18 months in 1995, he shares a vast array of hilarious and eye-opening ...