Insmed has launched a first-in-human Phase 1 trial testing its experimental ALS gene therapy INS1202 in people with the disease.

Microglia (immune cells) and the RANK protein are essential for triggering puberty and maintaining fertility in the brain.

Fungi have quietly shaped the trajectory of human civilization, from the diets of Paleolithic foragers to the beer in modern glasses and the experimental psychiatric drugs now in clinical trials. The ...

For two centuries, every system built to serve humanity — supply chains, healthcare, finance, energy, food, shelter — has failed the same test: matching real hu ...

Artificial intelligence (AI) has high strategic importance within biopharma marketing, sales, and commercialisation and nearly six in 10 pharma leaders report seeing 2x ROI from AI initiatives within ...

New research advances genetic diagnosisDemonstrates the potential to expand equitable access to treatment for patients living with rare inherited metabolic and neurodegenerative diseasesBALTIMORE ...

Mutations that cause spinal muscular atrophy (SMA) may lead to abnormalities in the development of cells in the spinal cord, a study found.

Interim analysis of Phase 1b clinical study of GT-02287, including biomarker and clinical endpoints, will be presented in oral symposium ...