The FDA has relaxed a clinical hold on clinical trials of Novartis' intrathecal formulation of spinal muscular atrophy (SMA) gene therapy Zolgensma, allowing a new phase 3 trial to get underway.

TerSera Therapeutics LLC today announced that it has completed the previously announced sale of its Infusion Specialty Therapies Business Unit (IST), including two specialty medications, Prialt(R) ...

Pages Latest Report] According to a market research study published by Custom Market Insights, the demand analysis of Global Amyotrophic Lateral Sclerosis Therapeutics Market size & share revenue was ...

The world’s first international patient, who received intrathecal gene therapy at Medcare Royal Hospital in Dubai, UAE, alongside their parents and the hospital team. Image: Supplied Medcare Women & ...

DUBAI, United Arab Emirates, December 30, 2025--(BUSINESS WIRE)--Medcare Women & Children Hospital has successfully administered a pioneering intrathecal gene therapy for Spinal Muscular Atrophy (SMA) ...

A preliminary investigation by the Chongqing Municipal Health Commission has found that a doctor at the Chongqing Medical University Children's Hospital injected a child patient with a drug that was ...

Novartis has received an FDA approval for Itvisma, a new version of the company’s gene therapy Zolgensma, to treat older patients with spinal muscular atrophy (SMA). The approval comes more than six ...

The FDA approved the intrathecal gene therapy onasemnogene abeparvovec (Itvisma) to treat spinal muscular atrophy (SMA) in adults and pediatric patients 2 years and older with a confirmed mutation in ...

Cytarabine is a type of chemotherapy. Cytarabine is also known as Ara C or cytosine arabinoside. Your doctor gives you the drug during a procedure called a lumbar puncture . They inject cytarabine ...

Biogen's acquisition of Alcyone Therapeutics focuses on advancing the ThecaFlex DRx system for intrathecal delivery of antisense oligonucleotides. The ThecaFlex DRx system provides an alternative to ...

Suggested remit: To appraise the clinical and cost effectiveness of intrathecal onasemnogene abeparvovec within its marketing authorisation for treating spinal muscular atrophy. Anticipate the topic ...

Baclofen (Gablofen, Lioresal, Ozobax) is a medication that treats stiff muscles and spasms, a condition called spasticity, that can happen to people with multiple sclerosis (MS) and other nerve ...