Genentech has stopped developing emugrobart after trial results showed no consistent benefit when added to Evrysdi in people ...

In 2018, when Nell Choi was 9 years old, she began experiencing symptoms that led to hospitalization and a diagnosis of ...

The movement-related benefits of Itvisma were maintained or continued to deepen over about 15 months after treatment, trial ...

Columnist Sherry Toh usually cringes at people who stare, but a performative art project taught her something new about ...

Up to three years of Evrysdi treatment appears safe and may help presymptomatic children with SMA reach and maintain key milestones.

Share this page with email Share this page on Facebook Share this page on X Share this page on Reddit Print Preferred Source on Google It is always an interesting and fun challenge to navigate my ...

High doses of Spinraza may help stabilize or improve motor function for many people with SMA, per pooled clinical trial ...

Salanersen, a treatment candidate for spinal muscular atrophy (SMA) now in clinical testing, is safe and was shown to stabilize or improve motor function over at least one year of follow-up in ...

Columnist Ari Anderson recently enjoyed six weeks free from searching for new members of his nursing staff. Now, he's aiming ...